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Orphan Drug
Ocelot’s Rare Kidney Disease Candidate Receives Orphan Drug Designation Going Into Phase 2 Trials
2022-08-23
Three Companies Received Orphan Drug Designations in One Day To Treat Rare Cancers
2022-06-20
The FDA Granted These Three Companies Orphan Drug Designations in One Day
2022-05-13
Telix Granted FDA Orphan Drug Designation for Bone Marrow Conditioning Treatment
2022-03-29
Applied Therapeutics’ Galactosemia Program Stumbles Again after FDA Requests for More Data
2022-01-04
FDA Greenlights Eton and Diurnal’s Orphan Drug for Pediatric Patients
2020-10-04
Investigational Gene Therapy for Cystinosis Obtains FDA’s Orphan Drug Designation
2020-03-10
Weekly in Asia|Nov-2
2019-11-27
Sangamo’s Shares Goes up after the Announcement of Investigational Hemophilia A Gene Therapy Results
2019-07-19
LATEST
Kaiser’s Data Breach: 13.4 Million Affected in Healthcare Conglomerates Privacy Crisis
2024-04-26
Mechanisms of Allograft Rejection: Insights from Behind the Scenes
2024-04-25
ImmunityBio’s ANKTIVA® Granted FDA Approval: Breakthrough IL-15 Receptor Agonist First-in-Class for BCG-Unresponsive Non-Muscle Invasive Bladder Cancer
2024-04-24
Takeda, Astellas, and Sumitomo Mitsui Banking Declare Agreement For Early Drug Discovery Program Incubation in Joint Venture
2024-04-23
Ochre Bio Announces Partnership with Boehringer Ingelheim to Develop Novel Regenerative Treatments for Patients with Advanced Liver Disease
2024-04-22
Earth Day Awareness: Hospitals Embrace Sustainability Efforts
2024-04-22
WHO Raises Alarm: Bird Flu Threat to Humans an ‘Enormous Concern’
2024-04-19
EVENT
2024-04-27
2024 Biomedical Final Pitch Competition
Room DA1620, Dana Building, Dana-Farber Cancer Institute, 99 Jimmy Fund Way, Boston, MA 02115
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